Biblio
2023
Li C, Georgakopoulou A, Newby GA, Chen PJ, Everette KA, Paschoudi K, Vlachaki E, Gil S, Anderson AK, Koob T, et al. In vivo HSC prime editing rescues Sickle Cell Disease in a mouse model. Blood. 2023.
2018
Wang H, Georgakopoulou A, Psatha N, Li C, Capsali C, Samal HBhusan, Anagnostopoulos A, Ehrhardt A, Izsvák Z, Papayannopoulou T, et al. In vivo hematopoietic stem cell gene therapy ameliorates murine thalassemia intermedia. J Clin Invest. 2018.